Therapeutics for Rare and Neglected Diseases

Metadata Updated: March 8, 2017

There are more than 6,500 identified rare and neglected diseases, yet only about 250 treatments are available for these conditions. The limited numbers of patients can make gathering information and designing drug studies difficult. As a result, scientists often know little about the symptoms and biology of these conditions. Also, some private companies may find it difficult to justify the cost of developing drugs for such small rare disease markets.The Therapeutics for Rare and Neglected Diseases (TRND) program is designed to combat these challenges. Its mission is to encourage and speed the development of new treatments for diseases with high unmet medical needs. TRND stimulates therapeutic development research collaborations among NIH and academic scientists, nonprofit organizations, and pharmaceutical and biotechnology companies working on rare and neglected illnesses. The program provides expertise and resources, working with research partners to move therapeutics through pre-clinical testing, including plans for clinical trials and submission of an IND application to the Food and Drug Administration. These efforts effectively [HTML_REMOVED]de-risk[HTML_REMOVED] therapeutic candidates and make them more attractive for adoption by outside business partners.

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Public: This dataset is intended for public access and use. License: No license information was provided. If this work was prepared by an officer or employee of the United States government as part of that person's official duties it is considered a U.S. Government Work.

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Metadata Created Date March 8, 2017
Metadata Updated Date March 8, 2017

Metadata Source

Harvested from Federal Laboratory Consortium Data.json

Additional Metadata

Resource Type Dataset
Metadata Created Date March 8, 2017
Metadata Updated Date March 8, 2017
Publisher Federal Laboratory Consortium
Unique Identifier 5B70D96B-1939-42E1-8DF4-1F8D1CBE8F3C
Lili Portilla
Maintainer Email
Public Access Level public
Address1 9800 Medical Center Drive, Building B, Room B3005
Metadata Context
Schema Version
Catalog Describedby
Harvest Object Id f7bbf07e-2503-4e9b-807e-08895289c052
Harvest Source Id 5859cfed-553c-48de-a478-b67b5225f6fc
Harvest Source Title Federal Laboratory Consortium Data.json
Phone 301-217-2589
Postalcode 20850
Sizesqft 0
Source Datajson Identifier True
Source Hash 2b1c87942b7b115125eb4116c37003ed7fb73c59
Source Schema Version 1.1
Statecode MD

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